Publication
10/04/2022
Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors.
Horiuchi M, Hinderer CJ, Greig JA, Dyer C, Buza EL, Bell P, Chichester JA, Hayashi PM, Yan H, Goode T, Wilson JM
Molecular Therapy. Methods & Clinical Development
Publication
3/22/2022
Efficacy and Safety of a Krabbe Disease Gene Therapy.
Hordeaux J, Jeffrey BA, Jian J, Choudhury GR, Michalson K, Mitchell TW, Buza EL, Chichester J, Dyer C, Bagel J, Vite CH, Bradbury AM, Wilson JM
Human Gene Therapy
