Publication 10/15/2021 Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Hemophilia A. Greig JA, Smith MK, Nordin JML, Goode T, Chroscinski EA, Buza EL, Schmidt N, Kattenhorn LM, Wadsworth S, Wilson JM Human Gene Therapy
Publication 8/17/2021 Muscle-directed AAV gene therapy rescues the maple syrup urine disease phenotype in a mouse model. Greig JA, Jennis M, Dandekar A, Chorazeczewski JK, Smith MK, Ashley SN, Yan H, Wilson JM Molecular Genetics And Metabolism
