Publication
10/12/2020
A single injection of an optimized AAV vector into cerebrospinal fluid corrects neurological disease in a murine model of GM1 gangliosidosis.
Hinderer C, Nosratbakhsh B, Katz N, Wilson JM
Human Gene Therapy
Publication
7/31/2020
Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology
Hordeaux J, Buza EL, Dyer C, Goode T, Mitchell TW, Richman L, Denton N, Hinderer C, Katz N, Schmid R, Miller R, Choudhury GR, Horiuchi M, Nambiar K, Yan H, Li M, Wilson JM
Human Gene Therapy
Publication
4/18/2020
Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration.
Hinderer C, Katz N, Dyer C, Goode T, Johansson J, Bell P, Richman L, Buza E, Wilson JM
Molecular Therapy. Methods & Clinical Development
