Publication 12/28/2019

Ionizable lipid nanoparticles encapsulating barcoded mRNA for accelerated in vivo delivery screening.

Guimaraes PPG, Zhang R, Spektor R, Tan M, Chung A, Billingsley MM, El-Mayta R, Riley RS, Wang L, Wilson JM, Mitchell MJ

Journal Of Controlled Release : Official Journal Of The Controlled Release Society

Publication 12/01/2019

TLR9 signaling mediates adaptive immunity following systemic AAV gene therapy.

Ashley SN, Somanathan S, Giles AR, Wilson JM

Cellular Immunology

Publication 11/25/2019

Adeno-associated virus-mediated expression of human butyrylcholinesterase to treat organophosphate poisoning.

Gupta V, Cadieux CL, McMenamin D, Medina-Jaszek CA, Arif M, Ahonkhai O, Wielechowski E, Taheri M, Che Y, Goode T, Limberis MP, Li M, Cerasoli DM, Tretiakova AP, Wilson JM

Plos One

Publication 9/01/2019

Breakthrough to Bedside: Bringing Gene Therapy to Neuromuscular Diseases.

Wilson JM

Human Gene Therapy. Clinical Development

Publication 6/27/2019

CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice.

Wang L, Yang Y, Breton CA, White J, Zhang J, Che Y, Saveliev A, McMenamin D, He Z, Latshaw C, Li M, Wilson JM

Blood

Publication 6/01/2019

Cycling at the Frontiers of Gene Therapy.

Wilson JM

Human Gene Therapy. Clinical Development