Publication
12/28/2019
Ionizable lipid nanoparticles encapsulating barcoded mRNA for accelerated in vivo delivery screening.
Guimaraes PPG, Zhang R, Spektor R, Tan M, Chung A, Billingsley MM, El-Mayta R, Riley RS, Wang L, Wilson JM, Mitchell MJ
Journal Of Controlled Release : Official Journal Of The Controlled Release Society
Publication
12/01/2019
TLR9 signaling mediates adaptive immunity following systemic AAV gene therapy.
Ashley SN, Somanathan S, Giles AR, Wilson JM
Cellular Immunology
Publication
11/25/2019
Adeno-associated virus-mediated expression of human butyrylcholinesterase to treat organophosphate poisoning.
Gupta V, Cadieux CL, McMenamin D, Medina-Jaszek CA, Arif M, Ahonkhai O, Wielechowski E, Taheri M, Che Y, Goode T, Limberis MP, Li M, Cerasoli DM, Tretiakova AP, Wilson JM
Plos One
Publication
9/01/2019
Breakthrough to Bedside: Bringing Gene Therapy to Neuromuscular Diseases.
Wilson JM
Human Gene Therapy. Clinical Development
Publication
6/27/2019
CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice.
Wang L, Yang Y, Breton CA, White J, Zhang J, Che Y, Saveliev A, McMenamin D, He Z, Latshaw C, Li M, Wilson JM
Blood
Publication
6/01/2019
Cycling at the Frontiers of Gene Therapy.
Wilson JM
Human Gene Therapy. Clinical Development