Publication
12/05/2018
AAV8 Gene Therapy for Crigler-Najjar Syndrome in Macaques Elicited Transgene T Cell Responses That Are Resident to the Liver.
Greig JA, Calcedo R, Kuri-Cervantes L, Nordin JML, Albrecht J, Bote E, Goode T, Chroscinski EA, Bell P, Richman LK, Betts MR, Wilson JM
Molecular Therapy. Methods & Clinical Development
Publication
8/28/2018
Adeno-associated viral gene therapy corrects a mouse model of argininosuccinic aciduria.
Ashley SN, Nordin JML, Buza EL, Greig JA, Wilson JM
Molecular Genetics And Metabolism
Publication
7/21/2018
Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome.
Greig JA, Nordin JML, Draper C, McMenamin D, Chroscinski EA, Bell P, Gray JT, Richman LK, Wilson JM
Molecular Therapy Methods And Clinical Development
Publication
2/16/2018
AAV8 Gene Therapy Rescues the Newborn Phenotype of a Mouse Model of Crigler-Najjar.
Greig JA, Nordin JML, Draper C, Bell P, Wilson JM
Human Gene Therapy