Skip navigation
Perelman School of Medicine at the University of Pennsylvania gtp-logo_ColorKnockoutNavy GENE THERAPY PROGRAM Navigate to home page
  • Home
  • About Us
  • The Wilson Lab
  • Vector Core
  • Our Team
  • News
  • Publications
  • Careers
  • Contact

Filter by year:

  • 2004
  • 2005
  • 2006
  • 2007
  • 2009
  • 2010
  • 2011
  • 2012
  • 2013
  • 2014
  • 2015
  • 2016
  • Deselect 2017
  • 2018
  • 2019
  • 2020
  • 2021
  • 2022
  • 2023

Filter by author:

  • Batshaw ML
  • Deselect Bell P
  • Calcedo R
  • Chen SJ
  • Dalla Corte A
  • de Souza CFM
  • Giugliani R
  • Greig JA
  • He Z
  • Hinderer C
  • Katz N
  • Limberis MP
  • Louboutin JP
  • Lund TC
  • Mesaros C
  • Morizono H
  • Nayal M
  • Orchard PJ
  • Pumbo E
  • Rader DJ
  • Tolar J
  • Wang L
  • Weng L
  • White J
  • Wilson JM
  • Yu H

Publication 10/01/2017

Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis.

Hinderer C, Katz N, Louboutin JP, Bell P, Tolar J, Orchard PJ, Lund TC, Nayal M, Weng L, Mesaros C, de Souza CFM, Dalla Corte A, Giugliani R, Wilson JM

Human Molecular Genetics

Publication 4/01/2017

AAV gene therapy corrects OTC deficiency and prevents liver fibrosis in aged OTC-knock out heterozygous mice.

Wang L, Bell P, Morizono H, He Z, Pumbo E, Yu H, White J, Batshaw ML, Wilson JM

Molecular Genetics And Metabolism

Publication 3/01/2017

Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial Hypercholesterolemia.

Greig JA, Limberis MP, Bell P, Chen SJ, Calcedo R, Rader DJ, Wilson JM

Human Gene Therapy. Clinical Development

Publication 3/01/2017

Non-Clinical Study Examining AAV8.TBG.hLDLR Vector-Associated Toxicity in Chow-Fed Wild-Type and LDLR+/- Rhesus Macaques.

Greig JA, Limberis MP, Bell P, Chen SJ, Calcedo R, Rader DJ, Wilson JM

Human Gene Therapy Clinical Development