Publication
12/01/2017
2017 Is the Year We Have Been Waiting For.
Wilson JM
Human Gene Therapy Clinical Development
Publication
12/01/2017
Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs.
Ye GJ, Komáromy AM, Zeiss C, Calcedo R, Harman CD, Koehl KL, Stewart GA, Iwabe S, Chiodo VA, Hauswirth WW, Aguirre GD, Chulay JD
Human Gene Therapy. Clinical Development
Publication
11/01/2017
Wnt10b and Dkk-1 gene therapy differentially influenced trabecular bone architecture, soft tissue integrity, and osteophytosis in a skeletally mature rat model of osteoarthritis.
Mason JB, Gurda BL, Hankenson KD, Harper LR, Carlson CS, Wilson JM, Richardson DW
Connective Tissue Research
Publication
10/01/2017
Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis.
Hinderer C, Katz N, Louboutin JP, Bell P, Tolar J, Orchard PJ, Lund TC, Nayal M, Weng L, Mesaros C, de Souza CFM, Dalla Corte A, Giugliani R, Wilson JM
Human Molecular Genetics
Publication
9/11/2017
Challenges in the gene therapy commercial ecosystem.
Kapoor R, Klueter T, Wilson JM
Nature Biotechnology
Publication
6/15/2017
Alternative Start Sites Downstream of Non-Sense Mutations Drive Antigen Presentation and Tolerance Induction to C-Terminal Epitopes.
Ashley SN, Somanathan S, Hinderer C, Arias M, McMenamin D, Draper C, Wilson JM
Journal Of Immunology