Publication 12/01/2017

2017 Is the Year We Have Been Waiting For.

Wilson JM

Human Gene Therapy Clinical Development

Publication 12/01/2017

Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs.

Ye GJ, Komáromy AM, Zeiss C, Calcedo R, Harman CD, Koehl KL, Stewart GA, Iwabe S, Chiodo VA, Hauswirth WW, Aguirre GD, Chulay JD

Human Gene Therapy. Clinical Development

Publication 11/01/2017

Wnt10b and Dkk-1 gene therapy differentially influenced trabecular bone architecture, soft tissue integrity, and osteophytosis in a skeletally mature rat model of osteoarthritis.

Mason JB, Gurda BL, Hankenson KD, Harper LR, Carlson CS, Wilson JM, Richardson DW

Connective Tissue Research

Publication 10/01/2017

Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis.

Hinderer C, Katz N, Louboutin JP, Bell P, Tolar J, Orchard PJ, Lund TC, Nayal M, Weng L, Mesaros C, de Souza CFM, Dalla Corte A, Giugliani R, Wilson JM

Human Molecular Genetics

Publication 9/11/2017

Challenges in the gene therapy commercial ecosystem.

Kapoor R, Klueter T, Wilson JM

Nature Biotechnology

Publication 6/15/2017

Alternative Start Sites Downstream of Non-Sense Mutations Drive Antigen Presentation and Tolerance Induction to C-Terminal Epitopes.

Ashley SN, Somanathan S, Hinderer C, Arias M, McMenamin D, Draper C, Wilson JM

Journal Of Immunology