Publication 12/01/2016 Effects of Self-Complementarity, Codon Optimization, Transgene, and Dose on Liver Transduction with AAV8. Bell P, Wang L, Chen SJ, Yu H, Zhu Y, Nayal M, He Z, White J, Lebel-Hagan D, Wilson JM Human Gene Therapy Methods
Publication 3/01/2016 A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice. Yang Y, Wang L, Bell P, McMenamin D, He Z, White J, Yu H, Xu C, Morizono H, Musunuru K, Batshaw ML, Wilson JM Nature Biotechnology