Publication
12/01/2015
Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids.
Wang L, Bell P, Somanathan S, Wang Q, He Z, Yu H, McMenamin D, Goode T, Calcedo R, Wilson JM
Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication
8/01/2015
Neonatal Systemic AAV Induces Tolerance to CNS Gene Therapy in MPS I Dogs and Nonhuman Primates.
Hinderer C, Bell P, Louboutin JP, Zhu Y, Yu H, Lin G, Choa R, Gurda BL, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Tarantal AF, Casal ML, Haskins ME, Wilson JM
Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication
6/17/2015
Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model.
Bissig-Choisat B, Wang L, Legras X, Saha PK, Chen L, Bell P, Pankowicz FP, Hill MC, Barzi M, Kettlun Leyton C, Leung HC, Kruse RL, Himes RW, Goss JA, Wilson JM, Chan L, Lagor WR, Bissig KD
Nature Communications
Publication
4/01/2015
Motor neuron transduction after intracisternal delivery of AAV9 in a cynomolgus macaque.
Bell P, Hinderer C, Louboutin JP, Yu H, Grant R, Bote E, Wilson JM
Human Gene Therapy Methods
