Publication
12/10/2014
Widespread gene transfer in the central nervous system of cynomolgus macaques following delivery of AAV9 into the cisterna magna.
Hinderer C, Bell P, Vite CH, Louboutin JP, Grant R, Bote E, Yu H, Pukenas B, Hurst R, Wilson JM
Molecular Therapy. Methods & Clinical Development
Publication
12/01/2014
Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis I.
Hinderer C, Bell P, Gurda BL, Wang Q, Louboutin JP, Zhu Y, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Haskins ME, Wilson JM
Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication
10/14/2014
Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I.
Hinderer C, Bell P, Gurda BL, Wang Q, Louboutin JP, Zhu Y, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Haskins ME, Wilson JM
Proceedings Of The National Academy Of Sciences Of The United States Of America
