Intramuscular injection of AAV8 in mice and macaques is associated with substantial hepatic targeting and transgene expression.
Greig JA, Peng H, Ohlstein J, Medina-Jaszek CA, Ahonkhai O, Mentzinger A, Grant RL, Roy S, Chen SJ, Bell P, Tretiakova AP, Wilson JM
Absolute determination of single-stranded and self-complementary adeno-associated viral vector genome titers by droplet digital PCR.
Lock M, Alvira MR, Chen SJ, Wilson JM
Human Gene Therapy Methods