We invite you to discover Human Gene Therapy Clinical Development, a peer-reviewed journal publishing preclinical research and clinical trial data for gene and cell therapies.

Publication 5/01/2012

Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector.

Wang L, Wang H, Bell P, McMenamin D, Wilson JM

Human Gene Therapy

Publication 4/01/2012

Sustained correction of OTC deficiency in spf( ash) mice using optimized self-complementary AAV2/8 vectors.

Wang L, Wang H, Morizono H, Bell P, Jones D, Lin J, McMenamin D, Yu H, Batshaw ML, Wilson JM

Gene Therapy

Publication 3/01/2012

Long-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skipping.

Bish LT, Sleeper MM, Forbes SC, Wang B, Reynolds C, Singletary GE, Trafny D, Morine KJ, Sanmiguel J, Cecchini S, Virag T, Vulin A, Beley C, Bogan J, Wilson JM, Vandenborne K, Kornegay JN, Walter GA, Kotin RM, Garcia L, Sweeney HL

Molecular Therapy : The Journal Of The American Society Of Gene Therapy

Publication 2/01/2012

Hepatocellular carcinoma in a research subject with ornithine transcarbamylase deficiency.

Wilson JM, Shchelochkov OA, Gallagher RC, Batshaw ML

Molecular Genetics And Metabolism

Publication 2/01/2012

Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.

Wang L, Morizono H, Lin J, Bell P, Jones D, McMenamin D, Yu H, Batshaw ML, Wilson JM

Molecular Genetics And Metabolism

Publication 2/01/2012

Analysis of particle content of recombinant adeno-associated virus serotype 8 vectors by ion-exchange chromatography.

Lock M, Alvira MR, Wilson JM

Human Gene Therapy Methods