Skip navigation
Perelman School of Medicine at the University of Pennsylvania gtp-logo_ColorKnockoutNavy GENE THERAPY PROGRAM Navigate to home page
  • Home
  • About Us
  • The Wilson Lab
  • Vector Core
  • Our Team
  • News
  • Publications
  • Careers
  • Contact

Filter by year:

  • 2010
  • 2011
  • Deselect 2012
  • 2014
  • 2015
  • 2016
  • 2017
  • 2018
  • 2020
  • 2021

Filter by author:

  • Batshaw ML
  • Bell P
  • Jones D
  • Lin J
  • McMenamin D
  • Morizono H
  • Wang H
  • Wang L
  • Wilson JM
  • Deselect Yu H

Publication 4/01/2012

Sustained correction of OTC deficiency in spf( ash) mice using optimized self-complementary AAV2/8 vectors.

Wang L, Wang H, Morizono H, Bell P, Jones D, Lin J, McMenamin D, Yu H, Batshaw ML, Wilson JM

Gene Therapy

Publication 2/01/2012

Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.

Wang L, Morizono H, Lin J, Bell P, Jones D, McMenamin D, Yu H, Batshaw ML, Wilson JM

Molecular Genetics And Metabolism