Publication
8/15/2012
RPGR-associated retinal degeneration in human X-linked RP and a murine model.
Huang WC, Wright AF, Roman AJ, Cideciyan AV, Manson FD, Gewaily DY, Schwartz SB, Sadigh S, Limberis MP, Bell P, Wilson JM, Swaroop A, Jacobson SG
Investigative Ophthalmology & Visual Science
Publication
5/01/2012
Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector.
Wang L, Wang H, Bell P, McMenamin D, Wilson JM
Human Gene Therapy
Publication
4/01/2012
Sustained correction of OTC deficiency in spf( ash) mice using optimized self-complementary AAV2/8 vectors.
Wang L, Wang H, Morizono H, Bell P, Jones D, Lin J, McMenamin D, Yu H, Batshaw ML, Wilson JM
Gene Therapy
Publication
2/01/2012
Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome.
Wang L, Morizono H, Lin J, Bell P, Jones D, McMenamin D, Yu H, Batshaw ML, Wilson JM
Molecular Genetics And Metabolism
