Publication
12/01/2010
Efficient gene transfer into the mouse lung by fetal intratracheal injection of rAAV2/6.2.
Carlon M, Toelen J, Van der Perren A, Vandenberghe LH, Reumers V, Sbragia L, Gijsbers R, Baekelandt V, Himmelreich U, Wilson JM, Deprest J, Debyser Z
Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication
10/19/2010
Gene therapy in a humanized mouse model of familial hypercholesterolemia leads to marked regression of atherosclerosis.
Kassim SH, Li H, Vandenberghe LH, Hinderer C, Bell P, Marchadier D, Wilson A, Cromley D, Redon V, Yu H, Wilson JM, Rader DJ
Plos One
Publication
10/01/2010
Rapid, simple, and versatile manufacturing of recombinant adeno-associated viral vectors at scale.
Lock M, Alvira M, Vandenberghe LH, Samanta A, Toelen J, Debyser Z, Wilson JM
Human Gene Therapy
Publication
10/01/2010
Efficient serotype-dependent release of functional vector into the culture medium during adeno-associated virus manufacturing.
Vandenberghe LH, Xiao R, Lock M, Lin J, Korn M, Wilson JM
Human Gene Therapy
Publication
1/01/2010
Systematic evaluation of AAV vectors for liver directed gene transfer in murine models.
Wang L, Wang H, Bell P, McCarter RJ, He J, Calcedo R, Vandenberghe LH, Morizono H, Batshaw ML, Wilson JM
Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication
1/01/2010
The pleiotropic effects of natural AAV infections on liver-directed gene transfer in macaques.
Wang L, Calcedo R, Wang H, Bell P, Grant R, Vandenberghe LH, Sanmiguel J, Morizono H, Batshaw ML, Wilson JM
Molecular Therapy : The Journal Of The American Society Of Gene Therapy