Publication
11/01/1999
Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.
Skorupa AF, Fisher KJ, Wilson JM, Parente MK, Wolfe JH
Experimental Neurology
Publication
7/01/1999
Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV.
Dudus L, Anand V, Acland GM, Chen SJ, Wilson JM, Fisher KJ, Maguire AM, Bennett J
Vision Research
