Publication 12/01/2014 Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis I. Hinderer C, Bell P, Gurda BL, Wang Q, Louboutin JP, Zhu Y, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Haskins ME, Wilson JM Molecular Therapy : The Journal Of The American Society Of Gene Therapy
Publication 10/14/2014 Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I. Hinderer C, Bell P, Gurda BL, Wang Q, Louboutin JP, Zhu Y, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Haskins ME, Wilson JM Proceedings Of The National Academy Of Sciences Of The United States Of America
