Publication
11/01/1995
A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia.
Grossman M, Rader DJ, Muller DW, Kolansky DM, Kozarsky K, Clark BJ 3rd, Stein EA, Lupien PJ, Brewer HB Jr, Raper SE
Nature Medicine
Publication
4/01/1994
Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia.
Grossman M, Raper SE, Kozarsky K, Stein EA, Engelhardt JF, Muller D, Lupien PJ, Wilson JM
Nature Genetics
