In vivo evaluation of adeno-associated virus gene transfer in airways of mice with acute or chronic respiratory infection.
Myint M, Limberis MP, Bell P, Somanathan S, Haczku A, Wilson JM, Diamond SL
Human Gene Therapy
AAV vectors expressing LDLR gain-of-function variants demonstrate increased efficacy in mouse models of familial hypercholesterolemia.
Somanathan S, Jacobs F, Wang Q, Hanlon AL, Wilson JM, Rader DJ