Publication
7/15/2021
Intranasal gene therapy to prevent infection by SARS-CoV-2 variants.
Sims JJ, Greig JA, Michalson KT, Lian S, Martino RA, Meggersee R, Turner KB, Nambiar K, Dyer C, Hinderer C, Horiuchi M, Yan H, Huang X, Chen SJ, Wilson JM
Plos Pathogens
Publication
10/12/2020
A single injection of an optimized AAV vector into cerebrospinal fluid corrects neurological disease in a murine model of GM1 gangliosidosis.
Hinderer C, Nosratbakhsh B, Katz N, Wilson JM
Human Gene Therapy
Publication
9/16/2020
Adeno-associated virus serotype 1-based gene therapy for FTD caused by GRN mutations.
Hinderer C, Miller R, Dyer C, Johansson J, Bell P, Buza E, Wilson JM
Annals Of Clinical And Translational Neurology
Publication
7/31/2020
Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology
Hordeaux J, Buza EL, Dyer C, Goode T, Mitchell TW, Richman L, Denton N, Hinderer C, Katz N, Schmid R, Miller R, Choudhury GR, Horiuchi M, Nambiar K, Yan H, Li M, Wilson JM
Human Gene Therapy
Publication
4/18/2020
Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration.
Hinderer C, Katz N, Dyer C, Goode T, Johansson J, Bell P, Richman L, Buza E, Wilson JM
Molecular Therapy. Methods & Clinical Development
Publication
4/24/2019
Safe and sustained expression of human iduronidase after adeno-associated virus 9 intrathecal administration in infant rhesus monkeys.
Hordeaux J, Hinderer C, Buza EL, Louboutin JP, Jahan T, Bell P, Chichester JA, Tarantal AF, Wilson JM
Human Gene Therapy