Publication 2/01/1996

Safety and feasibility of liver-directed ex vivo gene therapy for homozygous familial hypercholesterolemia.

Raper SE, Grossman M, Rader DJ, Thoene JG, Clark BJ 3rd, Kolansky DM, Muller DW, Wilson JM

Annals Of Surgery

Publication 11/01/1995

A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia.

Grossman M, Rader DJ, Muller DW, Kolansky DM, Kozarsky K, Clark BJ 3rd, Stein EA, Lupien PJ, Brewer HB Jr, Raper SE

Nature Medicine

Publication 3/01/1995

The low density lipoprotein receptor is not required for normal catabolism of Lp(a) in humans.

Rader DJ, Mann WA, Cain W, Kraft HG, Usher D, Zech LA, Hoeg JM, Davignon J, Lupien P, Grossman M

The Journal Of Clinical Investigation

Publication 5/01/1994

Gene therapy for cystic fibrosis using E1-deleted adenovirus: a phase I trial in the nasal cavity. The University of North Carolina at Chapel Hill.

Boucher RC, Knowles MR, Johnson LG, Olsen JC, Pickles R, Wilson JM, Engelhardt J, Yang Y, Grossman M

Human Gene Therapy

Publication 4/01/1994

Gene therapy of cystic fibrosis lung disease using E1 deleted adenoviruses: a phase I trial.

Wilson JM, Engelhardt JF, Grossman M, Simon RH, Yang Y

Human Gene Therapy

Publication 4/01/1994

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia.

Grossman M, Raper SE, Kozarsky K, Stein EA, Engelhardt JF, Muller D, Lupien PJ, Wilson JM

Nature Genetics