Publication
4/01/1994
Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia.
Grossman M, Raper SE, Kozarsky K, Stein EA, Engelhardt JF, Muller D, Lupien PJ, Wilson JM
Nature Genetics
Publication
2/01/1994
Expression of the cystic fibrosis gene in adult human lung.
Engelhardt JF, Zepeda M, Cohn JA, Yankaskas JR, Wilson JM
The Journal Of Clinical Investigation
Publication
12/01/1993
Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: biological efficacy study.
Engelhardt JF, Simon RH, Yang Y, Zepeda M, Weber-Pendleton S, Doranz B, Grossman M, Wilson JM
Human Gene Therapy
Publication
12/01/1993
Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: toxicity study.
Simon RH, Engelhardt JF, Yang Y, Zepeda M, Weber-Pendleton S, Grossman M, Wilson JM
Human Gene Therapy
Publication
8/01/1993
Molecular basis of defective anion transport in L cells expressing recombinant forms of CFTR.
Yang Y, Devor DC, Engelhardt JF, Ernst SA, Strong TV, Collins FS, Cohn JA, Frizzell RA, Wilson JM
Human Molecular Genetics
Publication
5/15/1993
An approach for treating the hepatobiliary disease of cystic fibrosis by somatic gene transfer.
Yang Y, Raper SE, Cohn JA, Engelhardt JF, Wilson JM
Proceedings Of The National Academy Of Sciences Of The United States Of America