Publication 4/01/1994

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia.

Grossman M, Raper SE, Kozarsky K, Stein EA, Engelhardt JF, Muller D, Lupien PJ, Wilson JM

Nature Genetics

Publication 2/01/1994

Expression of the cystic fibrosis gene in adult human lung.

Engelhardt JF, Zepeda M, Cohn JA, Yankaskas JR, Wilson JM

The Journal Of Clinical Investigation

Publication 12/01/1993

Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: biological efficacy study.

Engelhardt JF, Simon RH, Yang Y, Zepeda M, Weber-Pendleton S, Doranz B, Grossman M, Wilson JM

Human Gene Therapy

Publication 12/01/1993

Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: toxicity study.

Simon RH, Engelhardt JF, Yang Y, Zepeda M, Weber-Pendleton S, Grossman M, Wilson JM

Human Gene Therapy

Publication 8/01/1993

Molecular basis of defective anion transport in L cells expressing recombinant forms of CFTR.

Yang Y, Devor DC, Engelhardt JF, Ernst SA, Strong TV, Collins FS, Cohn JA, Frizzell RA, Wilson JM

Human Molecular Genetics

Publication 5/15/1993

An approach for treating the hepatobiliary disease of cystic fibrosis by somatic gene transfer.

Yang Y, Raper SE, Cohn JA, Engelhardt JF, Wilson JM

Proceedings Of The National Academy Of Sciences Of The United States Of America