Publication 10/15/2021 Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Hemophilia A. Greig JA, Smith MK, Nordin JML, Goode T, Chroscinski EA, Buza EL, Schmidt N, Kattenhorn LM, Wadsworth S, Wilson JM Human Gene Therapy
Publication 2/18/2021 Long-term stable reduction of low-density lipoprotein in nonhuman primates following in vivo genome editing of PCSK9. Wang L, Breton C, Warzecha CC, Bell P, Yan H, He Z, White J, Zhu Y, Li M, Buza EL, Jantz D, Wilson JM Molecular Therapy : The Journal Of The American Society Of Gene Therapy