Publication
8/17/2021
Muscle-directed AAV gene therapy rescues the maple syrup urine disease phenotype in a mouse model.
Greig JA, Jennis M, Dandekar A, Chorazeczewski JK, Smith MK, Ashley SN, Yan H, Wilson JM
Molecular Genetics And Metabolism
Publication
12/01/2019
TLR9 signaling mediates adaptive immunity following systemic AAV gene therapy.
Ashley SN, Somanathan S, Giles AR, Wilson JM
Cellular Immunology
Publication
3/01/2019
A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease.
Greig JA, Nordin JML, Smith MK, Ashley SN, Draper C, Zhu Y, Bell P, Buza EL, Wilson JM
Human Gene Therapy. Clinical Development
Publication
8/28/2018
Adeno-associated viral gene therapy corrects a mouse model of argininosuccinic aciduria.
Ashley SN, Nordin JML, Buza EL, Greig JA, Wilson JM
Molecular Genetics And Metabolism
Publication
6/15/2017
Alternative Start Sites Downstream of Non-Sense Mutations Drive Antigen Presentation and Tolerance Induction to C-Terminal Epitopes.
Ashley SN, Somanathan S, Hinderer C, Arias M, McMenamin D, Draper C, Wilson JM
Journal Of Immunology
Publication
7/01/2013
CpG-depleted adeno-associated virus vectors evade immune detection.
Faust SM, Bell P, Cutler BJ, Ashley SN, Zhu Y, Rabinowitz JE, Wilson JM
The Journal Of Clinical Investigation