Penn Medicine researchers have developed a new targeted approach to prevent a toxicity seen in the sensory neurons of dorsal root ganglia after gene therapy to treat neurological disorders. It’s an important hurdle to clear, as the field works toward more safe and effective gene therapies for patients with disorders like spinal muscular atrophy.
THE 7,600-JOB MOMENT Philadelphia is poised to become the epicenter of cell and gene therapy. Leaders like Dr. Steven Nichtberger have brought the local industry to a ‘tipping point.’
Allyson Berent is a specialty veterinarian in New York City. She treats animals that other doctors cannot help. When no good therapies are available, she invents one. Cats and dogs consumed almost all of her time — until six years ago, when her second daughter was born.
“Rare parents” are often left charting a world of unknowns. But their persistence has paid off with more advanced treatment options.
Dr. Jim Wilson has been selected by The Harrington Discovery Institute for a research award in the COVID-19 Rapid Response Initiative.
Renowned program led by James M. Wilson, MD, PhD, a leading expert in the technology platform used in the experimental vaccine, to conduct preclinical studies in joint research and development project with Massachusetts Eye and Ear and Massachusetts General Hospital.
