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9/04/2019

Passage Bio Closes $110 Million Series B Financing

Passage Bio, a genetic medicines company developing AAV-delivered gene therapies for the treatment of rare monogenic central nervous system (CNS) diseases, today announced the closing of a $110.0 million Series B financing.

9/03/2019

Passage Bio to Present at Morgan Stanley 17th Annual Global Healthcare Conference

Passage Bio, a genetic medicines company developing AAV-delivered gene therapies for the treatment of rare monogenic central nervous system diseases, today announced that Jill Quigley, Chief Operating Officer, will present at the Morgan Stanley 17th Annual Global Healthcare Conference on Monday, September 9th, 2019 at 8:10 a.m. ET in New York, NY.

8/13/2019

Passage Bio Announces Launch of Natural History Study to Evaluate Patients with GM1 Gangliosidosis

Passage Bio, a genetic medicines company developing AAV-delivered gene therapies for the treatment of rare monogenic central nervous system diseases, today announced the launch of a Natural History Study to evaluate patients with Type 1 and Type 2 GM1 gangliosidosis, a rare autosomal recessive genetic disorder that progressively destroys nerve cells in the brain and spinal cord. The study is being conducted by the Orphan Disease Center (ODC) in the Perelman School of Medicine at the University of Pennsylvania.

7/02/2019

Amicus Therapeutics and Catalent Biologics Enter Strategic Partnership for Gene Therapy Development and Manufacturing

Amicus has entered into a strategic manufacturing agreement with Paragon Gene Therapy for clinical manufacturing capabilities and capacity for multiple active preclinical lysosomal disorder programs that are currently in development in collaboration with the Gene Therapy Program at the University of Pennsylvania.

6/18/2019

Finally, Philly Has a Signature Industry to Kick-Start a Development Boom

What started in 2017 with one medical breakthrough is now poised to open the floodgates for an unprecedented development boom in Philadelphia.

6/08/2019

Philly Cyclists Ride to Raise Awareness for Rare Diseases

Bicyclists in Philadelphia are riding to raise awareness and money for rare diseases that affect some 200,000 Americans.