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Penn Medicine at the American Society of Gene and Cell Therapy 26th Annual Meeting

Nine researchers from the University of Pennsylvania’s Gene Therapy Program (GTP) presented abstracts highlighting their translational science and discovery research on gene therapy, gene editing, and adeno-associated virus (AAV) vector technology at the American Society of Cell and Gene Therapy (ASGCT)’s 26th Annual Meeting.

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Finding a Home for Orphan Diseases

Forty years after the Orphan Drug Act passed, researchers advance drug development for neglected rare conditions everywhere from the lab bench to backstage.

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