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Amicus Therapeutics and Catalent Biologics Enter Strategic Partnership for Gene Therapy Development and Manufacturing

Amicus has entered into a strategic manufacturing agreement with Paragon Gene Therapy for clinical manufacturing capabilities and capacity for multiple active preclinical lysosomal disorder programs that are currently in development in collaboration with the Gene Therapy Program at the University of Pennsylvania.


Finally, Philly Has a Signature Industry to Kick-Start a Development Boom

What started in 2017 with one medical breakthrough is now poised to open the floodgates for an unprecedented development boom in Philadelphia.


Philly Cyclists Ride to Raise Awareness for Rare Diseases

Bicyclists in Philadelphia are riding to raise awareness and money for rare diseases that affect some 200,000 Americans.


Passage Bio Announces Third Gene Therapy Development Program in Krabbe Disease and Supports Million Dreams Fundraising Gala

Check out this exciting news from our collaborators at Passage Bio!


Amicus Therapeutics and the University of Pennsylvania Announce Major Expansion of Gene Therapy Collaboration

Amicus Therapeutics and the Penn Gene Therapy Program markedly expand their research collaboration with plans to include most lysosomal storage disorders, 12 additional rare diseases, and $50M in Next Generation discovery efforts!


Amicus, Penn expand gene therapy collaboration in a big way

Our amazing expanded collaboration with Amicus Therapeutics has been featured in Philadelphia Business Journal! #raredisease #genetherapy